Search for Clinical Trial Results
Sandhoff Disease - 14 Studies Found
Status | Study |
Completed |
Study Name: Stem Cell Transplant for Inborn Errors of Metabolism Condition:
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Completed |
Study Name: Pharmacokinetics and Tolerability of Zavesca® (Miglustat) In Patients With Juvenile GM2 Gangliosidosis Condition: Gangliosidoses GM2 Date: 2007-01-04 Interventions: Drug: miglustat Target dose of 320 mg/m^2/day (divided in 3 doses) will be based on the Body Surface Are |
Completed |
Study Name: Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders Condition:
Date: 2012-06-20 Interventions:
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Terminated |
Study Name: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases Condition:
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